What does "gene therapy" aim to accomplish?

Gene therapy is primarily focused on modifying or replacing faulty genes in order to treat or prevent disease. This innovative approach targets the underlying genetic causes of various illnesses, particularly those that are inherited or caused by mutations in specific genes. By introducing, altering, or removing genetic material within a patient's cells, gene therapy can potentially correct the malfunctioning genes that lead to health issues, thereby alleviating or even curing the associated diseases.

For instance, in cases of genetic disorders like cystic fibrosis or muscular dystrophy, gene therapy aims to deliver a normal copy of the gene that is defective in the patient, thus restoring normal function. This targeted approach contrasts with traditional treatments that may only address symptoms rather than the root cause of the condition. By focusing on gene modification or replacement, gene therapy represents a revolutionary shift in how we can manage and treat genetic diseases, setting it apart from other options such as enhancement of physical performance, cloning for research purposes, or the unrealistic goal of completely eliminating all genetic disorders.